#beta thalassemia

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The First Crispr Treatment Is Making Its Way to Patients

The first CRISPR-based treatment, Casgevy, has been approved for sickle cell disease and beta thalassemia, marking a significant advance in gene-editing therapies.

Gene Therapies Could Transform Treatment of Rare Blood Disorders - News Center

Gene therapy shows promising results in treating rare genetic blood disorders like beta thalassemia and sickle cell disease.

Maimonides' holiday party brings comfort and cheer to pediatric patients * Brooklyn Paper

Maimonides Medical Center's holiday party enables pediatric patients to experience joy and normalcy, emphasizing the importance of mental well-being during treatment.

Vertex's CRISPR Gene Therapy Lands Another FDA Nod in a Rare Blood Disease

Vertex Pharmaceuticals and CRISPR Therapeutics' gene therapy, Casgevy, has received FDA approval as a treatment for beta thalassemia.
The therapy provides a one-time treatment option for transfusion-dependent beta thalassemia patients age 12 and older.

The First Crispr Treatment Is Making Its Way to Patients

The first CRISPR-based treatment, Casgevy, has been approved for sickle cell disease and beta thalassemia, marking a significant advance in gene-editing therapies.

Gene Therapies Could Transform Treatment of Rare Blood Disorders - News Center

Gene therapy shows promising results in treating rare genetic blood disorders like beta thalassemia and sickle cell disease.

Maimonides' holiday party brings comfort and cheer to pediatric patients * Brooklyn Paper

Maimonides Medical Center's holiday party enables pediatric patients to experience joy and normalcy, emphasizing the importance of mental well-being during treatment.

Vertex's CRISPR Gene Therapy Lands Another FDA Nod in a Rare Blood Disease

Vertex Pharmaceuticals and CRISPR Therapeutics' gene therapy, Casgevy, has received FDA approval as a treatment for beta thalassemia.
The therapy provides a one-time treatment option for transfusion-dependent beta thalassemia patients age 12 and older.
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